Moderated by: Sanaa Rizk
1. JSCDH-D-19-00042 "Evidence of the intrinsic coagulation pathway and contact system activation in sickle cell patients during steady state"
Corresponding author: Rafal Pawlinski Ph.D.
Other Authors: Michael W Henderson, Denis F Noubouossie, Erica M Sparkenbaugh, Anton Ilich, Nigel S Key
Speaker: Rafal Pawlinski, Ph.D.
2. JSCDH-D-19-00047 "Regulation of Fetal Hemoglobin through the Insulin Signaling Pathway"
Corresponding author: Vivien A. Sheehan, MD, PhD
Other Authors: Alireza Pakari, MD, Yankai Zhang, PhD, Alicia K Chang, MD, Ankush Goyal, Evadnie Rampersaud, PhD, Jonathan M Flanagan, PhD, Mitchell J Weiss, MD, PhD
Speaker: Vivien A. Sheehan, MD, PhD
3. JSCDH-D-19-00009 "LentiGlobin Gene Therapy in Patients with Sickle Cell Disease: Updated Interim Results from HGB-206"
Corresponding author: Lakshmanan Krishnamurti, MD
Other Authors: John F. Tisdale, MD, Julie Kanter, MD, Janet L. Kwiatkowski, MD, Markus Y. Mapara, MD, PhD, Manfred Schmidt, PhD, Alexandra L. Miller, Francis J. Pierciey, Wenmei Huang, PhD, Jean-Antoine Ribeil, MD, PhD, Alexis A. Thompson, MD, MPH, Mark C. Walters, MD.
Speaker: Lakshmanan Krishnamurti, MD
4. JSCDH-D-19-00012 "VOXELOTOR TREATMENT OF ADULTS AND ADOLESCENTS WITH SICKLE CELL DISEASE: RESULTS OF THE PHASE 3 HOPE TRIAL"
Corresponding author: Carolyn Hoppe
Other Authors: Elliot Vichinsky, Jo Howard, Kenneth I. Ataga, Videlis Nduba, Amal El Beshlawy, David L. Diuguid, Salam Al Kindi, Clark Brown, Hoda Hassab, Paul Telfer, Dimitris A. Tsitsikas, Selma Ünal, Julie Kanter, Miguel R. Abboud, Victor R. Gordeuk, Joshua Lehrer-Graiwer, Margaret Tonda, Allison Intondi, Russell E. Ware
Speaker: Ted Love, M.D.
5. JSCDH-D-19-00048 "A NOVEL NEXT-GENERATION SEQUENCING (NGS) BASED ASSAY FOR NON-INVASIVE PRENATAL TESTING OF SICKLE CELL DISEASE WITHOUT PATERNAL DNA"
Corresponding author: Vivien A. Sheehan, MD, PhD
Other Authors: Nelda Itzep, MD, Celeste K Kanne, BS, David Tsao, PhD, Oguzhan Attay, PhD
Speaker: Vivien A. Sheehan, MD, PhD
6. JSCDH-D-19-00049 " Strength of Clinical Transformation in Care for Patients with Sickle Cell Disease"
Corresponding author: Sanaa Rizk, MD, FACP
Other Authors: David Axelrod, MD, Gaye Riddick-Burden, CRNP, Elisabeth Congdon-MArtin, LSW, steven McKenzie, MD,PHD, Carol Haines, john McAna, PHD, Albert G. Crawford, PHD, lawrence Ward, MD
Speaker: Sanaa Rizk, MD, FACP